?? ????ACT001???????“???????????”??
????:1???????:??????????
2??????????
3?????
4??????????
5?????VX?
???????????????????2?6???????? (??? ??????)?????,???????????????????????????PI??ACT001,???????????(CDE)?????????????“??????????????”????????????????
??,?????“????”??????,???????????????????“????”????????????????????????????,?????????
??,ACT001???????????????????????????????????????????????????????,????????????????(???????)?????????,?????????????????????,ACT001?????????????????????,2021??????????
????,ACT001???????,?????????(ASCO)????????????????(SNO)??????????????????(ERS)????????????????????,????????????????????????????????????5???????,?????????????????????(FDA)????????????ACT001“??????????????”,????????
????????????????????????????,??“?”,??ACT001???????????2b/3?????????,??,???????????????????????????????????????????????????????????(???????????????????????) ????????????:????????